.Pharmacolibrary.Drugs.ATC.A.A16AB07 .Pharmacolibrary.Drugs.ATC.A.A16AB07| name: | AlglucosidaseAlfa |
| ATC code: | A16AB07 | route: | intravenous |
| n-compartments | 2 |
Alglucosidase alfa is a recombinant human acid alpha-glucosidase enzyme replacement therapy approved for the treatment of Pompe disease (glycogen storage disease type II), a rare genetic disorder caused by deficiency of the lysosomal enzyme acid alpha-glucosidase. It is administered to help reduce glycogen accumulation in tissues, primarily skeletal and cardiac muscle.
Pharmacokinetics in patients with Pompe disease, both infantile-onset and late-onset, after intravenous infusion. Estimates from published clinical studies in both pediatric and adult populations.