name: | Galsulfase |
ATC code: | A16AB08 | route: | intravenous |
n-compartments | 2 |
Galsulfase is a recombinant human N-acetylgalactosamine-4-sulfatase enzyme used in enzyme replacement therapy for patients with mucopolysaccharidosis type VI (MPS VI, Maroteaux-Lamy syndrome). It is approved for intravenous use to slow or reverse the accumulation of glycosaminoglycans in affected tissues.
Pharmacokinetic parameters in pediatric and adult patients with MPS VI receiving recommended doses.