name: | AvalglucosidaseAlfa |
ATC code: | A16AB22 | route: | intravenous |
n-compartments | 2 |
Avalglucosidase alfa is a recombinant human acid alpha-glucosidase enzyme indicated for long-term enzyme replacement therapy in patients with Pompe disease (acid alpha-glucosidase deficiency). It is approved for use in the treatment of late-onset Pompe disease.
Pharmacokinetic parameters reported in adult subjects with late-onset Pompe disease after intravenous administration.