modelP01CX04

Extends from Pharmacokinetic.Models.PK_2C_enteral.

Information

name:Miltefosine
ATC code:P01CX04
route:oral
compartments:2
dosage:50mg
volume of distribution:66L
clearance:1.7L/h
other parameters in model implementation

Miltefosine is an alkylphosphocholine drug that was originally developed as an anticancer agent, but is currently approved and primarily used for the oral treatment of leishmaniasis (visceral, cutaneous, and mucocutaneous), a neglected tropical protozoal disease. It is the first effective oral drug for leishmaniasis and is included in WHO’s Essential Medicines List.

Pharmacokinetics

Population pharmacokinetic parameters in adult Indian patients with visceral leishmaniasis following standard oral dosing.

References

  1. Ramisetty, BS, et al., & Wang, MZ (2024). Determining tissue distribution of the oral antileishmanial agent miltefosine: a physiologically-based pharmacokinetic modeling approach. Antimicrobial agents and chemotherapy 68(7) e0032824–None. DOI:10.1128/aac.00328-24 PUBMED:https://pubmed.ncbi.nlm.nih.gov/38842325

  2. Berman, J (2005). Miltefosine to treat leishmaniasis. Expert opinion on pharmacotherapy 6(8) 1381–1388. DOI:10.1517/14656566.6.8.1381 PUBMED:https://pubmed.ncbi.nlm.nih.gov/16013987

  3. Sundar, S, et al., & Berman, J (2003). Oral miltefosine treatment in children with mild to moderate Indian visceral leishmaniasis. The Pediatric infectious disease journal 22(5) 434–438. DOI:10.1097/01.inf.0000066877.72624.cb PUBMED:https://pubmed.ncbi.nlm.nih.gov/12792385

Parameters

TypeNameDefaultDescription
Modelica.Units.SI.Massweight (from PK_1C)75patient weight (kg)
Modelica.Units.SI.SpecificVolumeVdPerKg (from PK_1C)0.9Volume of distribution (L/kg)
Modelica.Units.SI.MassFractionF (from PK_1C)0.8bioavailiability (0-1)
Pharmacolibrary.Types.ClearanceCl (from PK_1C)20clearance
Modelica.Units.SI.TimeadminTime (from PK_1C)60first administration time (s)
Modelica.Units.SI.TimeadminDuration (from PK_1C)600administration duration (s)
Modelica.Units.SI.TimeadminPeriod (from PK_1C)8*60*60period of administration (default 8 hours)(s)
Pharmacolibrary.Types.MassadminMass (from PK_1C)1000administration mass (mg)
IntegeradminCount (from PK_1C)8number of dose administered (1)
Pharmacolibrary.Types.VolumeVd (from PK_1C)VdPerKg*weightVolume of distribution (m3)
Pharmacolibrary.Types.MassConcentrationCmin (from PK_1C)0.004minimal therapeutic range
Pharmacolibrary.Types.MassConcentrationCmax (from PK_1C)0.008minimal therapeutic range
Pharmacolibrary.Types.MassConcentrationCtox_peak (from PK_1C)0.012toxicity peak level
Pharmacolibrary.Types.MassConcentrationCtox_trough (from PK_1C)0.006toxicity trough level
Pharmacolibrary.Types.VolumeVdp (from PK_2C)VdpPerKg*weightVolume of distribution (m3)
Modelica.Units.SI.SpecificVolumeVdpPerKg (from PK_2C)0.9Volume of distribution peripheral(l/kg)
Pharmacolibrary.Types.Clearancek12 (from PK_2C)1intercompartmental C-P clearance
Pharmacolibrary.Types.Clearancek21 (from PK_2C)1intercompartmental P-C clearance
Pharmacolibrary.Types.TransferRateka (from PK_2C_enteral)0.016666666666666666first order absorption rate
Modelica.Units.SI.TimeTlag (from PK_2C_enteral)600delay between oral administration and absorption (default 10min)

Connectors

TypeNameDefaultDescription
Types.ConcentrationOutputC_central (from PK_1C)
Interfaces.ConcentrationPort_bcentralCPort (from PK_1C)
Interfaces.ConcentrationPort_bperipheralCPort (from PK_2C)
Pharmacolibrary.Types.ConcentrationOutputC_peripheral1 (from PK_2C)

Components

TypeNameDefaultDescription
Pharmacokinetic.NoPerfusedTissueCompartmentcentral (from PK_1C)
Pharmacokinetic.ClearanceDrivenEliminationelim (from PK_1C)
Sources.PeriodicDoseperiodicDose (from PK_1C)
Modelica.Units.SI.Timet1_2 (from PK_1C)elimination half-life
Pharmacolibrary.Pharmacokinetic.TransferFirstOrderNonSymtransfer (from PK_2C)
Pharmacolibrary.Pharmacokinetic.NoPerfusedTissueCompartmentperipheral (from PK_2C)

Revisions

  • 06/2025 Tomas Kulhanek, generated model from data extracted from PUBMED, DrugBank and LLM(GPT4.1)