modelCiltacabtageneAutoleucel

Diagram of CiltacabtageneAutoleucel

Extends from Pharmacolibrary.Drugs.ATC.L.L01XL05.

Information

name:CiltacabtageneAutoleucel
ATC code:L01XL05
route:intravenous
compartments:0
dosage:0.75mg
volume of distribution:1L
clearance:0
other parameters in model implementation

Ciltacabtagene autoleucel is a BCMA-directed, genetically modified autologous T cell immunotherapy (CAR-T therapy), indicated for the treatment of adult patients with relapsed or refractory multiple myeloma. It is approved in the United States and several other countries for use in patients who have received at least four prior lines of therapy.

Pharmacokinetics

No conventional pharmacokinetic parameters such as clearance, volume of distribution, or compartment modeling are typically reported for ciltacabtagene autoleucel, as it is a cell-based gene therapy. Available data is limited to cellular expansion and persistence in blood of adult patients with relapsed or refractory multiple myeloma.

References

  1. Wu, LS, et al., & Zhou, H (2022). Population-based cellular kinetic characterization of ciltacabtagene autoleucel in subjects with relapsed or refractory multiple myeloma. Clinical and translational science 15(12) 3000–3011. DOI:10.1111/cts.13421 PUBMED:https://pubmed.ncbi.nlm.nih.gov/36204820

Parameters

TypeNameDefaultDescription
Modelica.Units.SI.Massweight (from PK_1C)75patient weight (kg)
Modelica.Units.SI.SpecificVolumeVdPerKg (from PK_1C)0.9Volume of distribution (L/kg)
Modelica.Units.SI.MassFractionF (from PK_1C)0.8bioavailiability (0-1)
Pharmacolibrary.Types.ClearanceCl (from PK_1C)20clearance
Modelica.Units.SI.TimeadminTime (from PK_1C)60first administration time (s)
Modelica.Units.SI.TimeadminDuration (from PK_1C)600administration duration (s)
Modelica.Units.SI.TimeadminPeriod (from PK_1C)8*60*60period of administration (default 8 hours)(s)
Pharmacolibrary.Types.MassadminMass (from PK_1C)1000administration mass (mg)
IntegeradminCount (from PK_1C)8number of dose administered (1)
Pharmacolibrary.Types.VolumeVd (from PK_1C)VdPerKg*weightVolume of distribution (m3)
Pharmacolibrary.Types.MassConcentrationCmin (from PK_1C)0.004minimal therapeutic range
Pharmacolibrary.Types.MassConcentrationCmax (from PK_1C)0.008minimal therapeutic range
Pharmacolibrary.Types.MassConcentrationCtox_peak (from PK_1C)0.012toxicity peak level
Pharmacolibrary.Types.MassConcentrationCtox_trough (from PK_1C)0.006toxicity trough level

Connectors

TypeNameDefaultDescription
Types.ConcentrationOutputC_central (from PK_1C)
Interfaces.ConcentrationPort_bcentralCPort (from PK_1C)

Components

TypeNameDefaultDescription
Pharmacokinetic.NoPerfusedTissueCompartmentcentral (from PK_1C)
Pharmacokinetic.ClearanceDrivenEliminationelim (from PK_1C)
Sources.PeriodicDoseperiodicDose (from PK_1C)
Modelica.Units.SI.Timet1_2 (from PK_1C)elimination half-life

Revisions

  • 06/2025 Tomas Kulhanek, generated model from data extracted from PUBMED, DrugBank and LLM(GPT4.1)