.Pharmacolibrary.Drugs.A_AlimentaryTractAndMetabolism.A16A_OtherAlimentaryTractAndMetabolismProducts.A16AB15_VelmanaseAlfa.VelmanaseAlfa .Pharmacolibrary.Drugs.A_AlimentaryTractAndMetabolism.A16A_OtherAlimentaryTractAndMetabolismProducts.A16AB15_VelmanaseAlfa.VelmanaseAlfa| name: | VelmanaseAlfa |
| ATC code: | A16AB15 | route: | intravenous |
| n-compartments | 2 |
Velmanase alfa is a recombinant human alpha-mannosidase enzyme replacement therapy used for the treatment of alpha-mannosidosis, a rare lysosomal storage disorder. It is approved in the European Union for long-term enzyme replacement therapy in non-neurological manifestations of mild to moderate alpha-mannosidosis.
Pharmacokinetic parameters reported for adult and pediatric patients (both sexes) with alpha-mannosidosis following intravenous infusion of velmanase alfa (recombinant human alpha-mannosidase).